| Accession |
PRJCA024236 |
| Title |
This is a single arm, multicenter study in participants who are diagnosed with Gaucher disease type III |
| Relevance |
Medical |
| Data types |
Variation
|
| Organisms |
Homo sapiens
|
| Description |
Approximately 12 participants will be assigned to study intervention in the study in order to yield at least 10 evaluable patients at the end of 52 weeks. Patient drop-out rate will be monitored for the purpose of adjusting the sample size. |
| Sample scope |
Single cell |
| Release date |
2024-04-01 |
| Grants |
| Agency |
program |
Grant ID |
Grant title |
| No funding support
|
|
|
|
|
|
| Submitter |
zhengqing
qiu (zhengqingqiu33@aliyun.com)
|
| Organization |
Peking Union Medical College Hospital- Chinese Academy of Medical Sciences-Peking Union Medical College |
| Submission date |
2024-03-12 |
