Introduction to a supplement on innovative approaches to studying health outcomes in rare diseases.
Aaron S Kesselheim, Joshua J Gagne
Author Information
- Aaron S Kesselheim: From the Program On Regulation, Therapeutics, And Law, Division of Pharmacoepidemiology and Pharmacoeconomics, Department of Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, MA, USA, akesselheim@partners.org.
No abstract text available.
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Humans
Outcome Assessment, Health Care
Rare Diseases
